Pitt Pediatrics congratulates the following faculty on their receipt of new grants during the third quarter of fiscal year 2021:
NIH and Other Federal
Eric S. Goetzman, PhD
Division of Genetic and Genomic Medicine
Optimizing medium-chain lipids for the treatment of long-chain fatty acid oxidation disorders
National Institutes of Health, 1R01HD103602-01
03/16/2021-02/28/2026
Elizabeth Miller, MD, PhD, FSAHM
Division of Adolescent and Young Adult Medicine
Creating Peace: community-based youth violence prevention to address racism
National Institutes of Health, 5R01MD013797-03
03/01/2021-01/31/2023
Kathryn Seraphin Torok, MD
Division of Rheumatology
Ancillary Studies to Define Dysregulated Immune and Fibrotic Pathways in a Well-Characterized Morphea Cohort
National Institutes of Health, 1R01AR078560-01
03/01/2021-01/31/2025
Jerry Vockley, MD, PhD, FACMG
Division of Genetic and Genomic Medicine
Characterization of Branched Chain Amino Acid Metabolism and Its Deficiency
National Institutes of Health, 2R01DK109907-05A1
03/01/2021-02/28/2025
Other
Silva Arslanian, MD
Center for Pediatric Research in Obesity and Metabolism
PIONEER TEENS: Efficacy and safety of oral semaglutide versus placebo both in combination with metformin and/or basal insulin in children and adolescents with type 2 diabetes
Novo Nordisk Pharmaceuticals, Inc.
Catalina Cleves-Bayon, MD
Division of Neurology and Child Development Unit
A Randomized, Double-Blind, Placebo-Controlled Study of Galcanezumab in Patients 6 to 17 Years of Age with Chronic Migraine - the REBUILD-2 Study
Eli Lilly
Oscar Escobar, MD
Division of Endocrinology
A Multicenter, 6-Month, Randomized, Open-Label, Active Control, Parallel Arm, Phase 2b Study of Daily Oral LUM201 in Naïve-to-Treatment, Prepubertal Children with Growth Hormone Deficiency (GHD) to Evaluate Predictive Enrichment Marker (PEM)
Lumos Pharmaceuticals
Geoffrey Kurland, MD
Division of Pulmonology
ELX/TEZ/IVA Expanded Access Program for Patients 6 Through 11 Years of Age With Cystic Fibrosis Who Have At Least One F508Del Mutation
Vertex
Patrick J. Mckiernan, MD
Division of Gastroenterology, Hepatology, and Nutrition
Expanded Access Protocol (EAP): Odevicibat (A4250) for the Treatment of Progressive Familial Intrahepatic Cholestasis) PED-20-022
Albireo AB
Robert H. Squires, MD, FAAP, FAASLD
Division of Gastroeneterolgy, Hepatology, and Nutrition
PED-20-019 Randomized, Double-blinded, Placebo-Controlled Phase 2 Study to Evaluate the EfficacPy and Safety of Maralixibat in the Treatment of Subjects with Biliary Atresia after Hepatoportoenterostomy
Mirium Pharmaceuticals, Inc.
Jessie L. Barnum, MD
Division of Blood and Marrow Transplantation and Cellular Therapies
Treatment of Globoid Cell Leukodystrophy by Combined Adeno-associated Virus Mediated Gene Transfer and Hematopoietic Stem Cell Transplantation
Forge Biologics
Maria Luisa Escolar, MD, MS
Division of Genetic and Genomic Medicine
ABT-003: A Phase I/II Open Label, Single-dose, Gene Transfer Study of scAAV9.U1a.hSGSH (ABO-102) in Patients with Middle and Advanced Phases of MPS IIIA Disease
Abeona Therapeutics
Maria Luisa Escolar, MD, MS
Division of Genetic and Genomic Medicine
An Open-label, Phase 1/2 Study to Evaluate the Safety of PR001A in Infants with Type 2 Gaucher Disease
Prevail Therapeutics, Inc.
Nader Shaikh, MD, MPH
Division of General Academic Pediatrics
Severity of SARS-CoV-2 infection in household contacts of patients with COVID-19: The role of epigenetics
Merck
Timothy R. Shope, MD, MPH
Division of General Academic Pediatrics
SARS-CoV-2 Surveillance in Child Care Centers
Merck
Jerry Vockley, MD, PhD, FACMG
Division of Genetic and Genomic Medicine
A Global, Phase 1/2, Open-label, Dose Optimization Study to Evaluate the Safety, Pharmacodynamics, and Pharmacokinetics of mRNA-3927 in Participants with Propionic Acidemia
Moderna TX, Inc.
Jerry Vockley, MD, PhD, FACMG
Division of Genetic and Genomic Medicine
A Phase 1b Randomized, Double Blinded, Placebo Controlled, Ascending Dose Study to Assess the Safety, Tolerability, and Pharmacokinetics of Single Doses of ARCT-810 in Clinically Stable Patients with Ornithine Transcarbamylase Deficiency
Arcturus Therapeutics, Ltd.
Carol A. Bertrand, PhD
Cystic Fibrosis Research Center
Correcting Pathogenic TGF beta Activity in the Airway
University of Virginia
Brian Feingold, MD, MS, FAHA
Division of Cardiology
MUSIC (Long-TerM OUtcomes after the Multisystem Inflammatory Syndrome In Children)
New England Research Institute - NERI
Philana Ling Lin, MD, MSc
Division of Infectious Diseases
Development of a Self Inactivating, Highly Effective TB Vaccine
National Institutes of Health
Edward V. Prochownik, MD, PhD
Division of Hematology-Oncology
Mitonuclear Communication During the Pathogenesis of Inflammatory Bowel Disease
National Institutes of Health
Jean M. Tersak, MD
Division of Hematology-Oncology
Project: One Time EOY, Integrated BIQSFP AAML1031- Echocardiogram Reports and Images
Children's Hospital of Philadelphia
Toby Debra Yanowitz, MD, MS
Division of Newborn Medicine
Stochastic vibro-tactile stimulation: A non-pharmacological intervention for abstinence and drug withdrawal in newborn infants
National Institutes of Health
Carla D. Chugani, PhD, LPC
Division of Adolescent and Young Adult Medicine
Social emotional learning curriculum and Teen Outreach Program
Homeless Children's Education Fund
Thomas G. Diacovo, MD, PhD, FACMG
Division of Newborn Medicine
Preterm Birth and Infant Mortality
Magee-Womens Research Institute and Foundation
Traci Marie Kazmerski, MD, MS
Division of Allergy and Immunology
Urinary Incontinence in Women with Cystic Fibrosis
Cystic Fibrosis Foundation
Kelly M. Bailey, MD, PhD
Division of Hematology-Oncology
Regulators of Immunosuppression in the Ewing Microenvironment
Alex's Lemonade Stand
Andrew P. Feranchak, MD
Division of Gastroenterology, Hepatology, and Nutrition
Mechanisms of Cholangiocyte Secretion and Cystic Fibrosis Liver Disease
Cystic Fibrosis Foundation
Traci Marie Kazmerski, MD, MS
Division of Allergy and Immunology
Parenthood and Cystic Fibrosis Planning Grant
Cystic Fibrosis Foundation
Lisa Maurer, MD, PhD
Division of Hematology-Oncology
DNA Damage Induced Immune Regulatin in Non-Hodgkin Lymphoma
Hyundai Hope on Wheels
Vikram Kalathur Raghu, MD, MS
Division of Gastroenterology, Hepatology, and Nutrition
Optimal Lipid Supplementation Strategy for the Prevention and Treatment of Parenteral Nutrition-Associated Liver Disease in Children with Intestinal Failure
ASPEN Foundation
Kristin N. Ray, MD, MS, FAAP
Division of General Academic Pediatrics
Family Health Survey and Database
Claude Washington Benedum Foundation